A Journey of Independence Amidst Uncertainty in Duchenne Treatment
By Editor • August 20, 2026 • 1 min read
Five years ago, we embarked on a transformative journey, moving my son into a college dorm, despite his Duchenne muscular dystrophy limiting his mobility.
As he prepares for his second year of graduate studies, we reflect on his resilience and the impact of Capricor's deramiocel.
Last week, the drug faced a setback when an FDA advisory committee voted against its effectiveness in stabilizing heart function in a mixed population, raising questions about the data's reliability.
Source: www.statnews.com
#Capricor #deramiocel #Duchenne muscular dystrophy #FDA #heart function